Catherine Skari

EHA2022 | Agios Presents New Data Supporting the Benefits of PYRUKYND®In Adults With PKD

Data were presented at the European Hematology Association (EHA) Annual Congress, hosted virtually and in person in Vienna on June…

Read More »

Promoting Adherence to Iron Chelation Treatment in Beta-Thalassemia Patients

Thalassaemia is one of the commonest inherited genetic disorders world-wide with around 25,000 births of the most severely affected transfusion…

Read More »

Sickle Cell Disease Related Mortality in Brazil, 2000-2018

Introduction There is a demand to update national mortality trends data related to sickle cell disease (SCD) in Brazil. This…

Read More »

l-glutamine, crizanlizumab, voxelotor, and cell-based therapy for adult sickle cell disease: Hype or hope?

For more than two decades, hydroxyurea was the only therapeutic agent approved by the Food and Drug Administration (FDA) for sickle cell disease (SCD).…

Read More »

Kidney Stones in Transfusion-Dependent Thalassemia: Prevalence and Risk Factors

As patients with transfusion-dependent thalassemia (TDT) are living longer, novel morbidities are being recognized. The purpose of this review is…

Read More »

Global Globin Network Consensus Paper: Classification and Stratified Roadmaps for Improved Thalassaemia Care and Prevention in 32 Countries

The Global Globin Network (GGN) is a project-wide initiative of the Human Variome/Global Variome Project (HVP) focusing on haemoglobinopathies to…

Read More »

Pregnancy Outcomes Among Women Affected with Thalassemia Traits

Objective To compare the maternal and perinatal outcomes between a group of pregnant women diagnosed with thalassemia traits and normal…

Read More »

Early Detection of Iron Overload Cardiomyopathy in Transfusion Dependent Thalassemia Patients in Sulaimaniyah City, Iraq

Lifelong blood transfusion is recommended for patients with transfusion-dependent thalassemia (TDT) that lead to iron overload and results in cardiomyopathy…

Read More »

NEW WHO REPORT | Effective TB, HIV, Viral Hepatitis Services For Refugees And Migrants Across The WHO European Region

International recommendations on effective services to treat tuberculosis (TB), HIV and viral hepatitis for refugees and migrants lack implementation across…

Read More »

Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease

BACKGROUND Sickle cell disease is characterized by the painful recurrence of vaso-occlusive events. Gene therapy with the use of LentiGlobin…

Read More »