Catherine Skari – Page 34

Aug- 2022 -

13 August

Safety and Efficacy of Mitapivat, an Oral Pyruvate Kinase Activator, in Adults with Non-Transfusion Dependent α-Thalassaemia or β-Thalassaemia: An Open-label, Multicentre, Phase 2 Study

Background: Patients with non-transfusion-dependent thalassaemia (NTDT), although they do not require regular blood transfusions for survival, can still accrue a heavy…

9 August

Scientific Literature

New Entity—Thalassemic Endocrine Disease: Major Beta-Thalassemia and Endocrine Involvement

Beta-thalassemia (BTH), a recessively inherited haemoglobin (Hb) disorder, causes iron overload (IO), extra-medullary haematopoiesis and bone marrow expansion with major…

3 August

Scientific Literature

2021 Thalassaemia International Federation Guidelines for the Management of Transfusion-dependent Thalassemia

Beta-thalassemia and particularly its transfusion-dependent form (TDT) is a demanding clinical condition, requiring life-long care and follow-up, ideally in specialized…

1 August

TIF Publications

A Short Guide for the Management of Transfusion-Dependent Thalassaemia (2nd edition – 2022)

Prepared by: Farmakis, D. Reviewed by: Eleſtheriou, A., Bain, B.

Jul- 2022 -

11 July

Scientific Literature

Frequency, Pattern, and Associations of Renal Iron Accumulation in Sickle/β-Thalassemia Patients

We evaluated frequency, pattern, and associations of renal iron accumulation in sickle/β-thalassemia. Thirty-three sickle/β-thalassemia patients (36.5 ± 14.7 years; 13 females), 14 homozygous…

Jun- 2022 -

18 June

News