Catherine Skari

NEW | Bluebirdbio Releases Resources For Patients On Gene Therapy Zynteglo®

To help people who are living with or caring for someone who has β-thalassaemia major get substantial information about Zynteglo®,…

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UNITED Onlus | The Italian Federation Of Thalassaemia Welcomes Newly Elected BoD

The assembly was held in the conference room of the Zone Hotel in Rome. The members of the new board…

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OUT NOW | 2021 TIF Annual Report Has Been Published

The 2021 Annual Report will cover the following and more: Message by TIF’s President and Executive Director  2021 in Numbers…

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THALASSAEMIA AND SICKLE CELL AUSTRALIA (TASCA) | Spring Newsletter 2022

Contents: Chair’s address Staff update TIF update TASCA Engagement In Memory of Lou Alborea TASCA kids’ page View the Newsletter…

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ADVANCED THERAPIES | Vertex, CRISPR To Submit Exa-Cel to FDA For β-Thalassaemia And Sickle Cell Disease

Vertex will submit its biologics licensing application (BLA) for exa-cel for rolling review, beginning in November 2022 and expects to…

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CDC | Many Children With Sickle Cell Anaemia In The US Not Receiving Lifesaving Screening And Treatment

According to a recent CDC study, fewer than half children with the disease in the US get the necessary screening,…

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CLINICAL NEWS | PYRUKYND® Receives Positive CHMP Opinion For The Treatment of PKD in Adults

PYRUKYND® is a first-in-class, oral PK activator that was recently approved by the U.S. Food and Drug Administration (FDA). If approved by the…

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Renal Dysfunction in Pediatric Patients in Iraq With β-Thalassemia Major and Intermedia

Background: With optimum transfusion and chelation therapy, the survival of β-thalassemia patients and the incidence of various complications, including renal…

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NEWSLETTER | Iranian Blood Transfusion Organization (IBTO) August 2022

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SAFER BLOOD | EU Patients Have Begun Receiving Transfusions With Hemanext ONE® RBC Processing & Storage System

Doctors have begun transfusing patients suffering from hematological malignancies using RBCs processed and stored with the Hemanext ONE® system, as part…

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