Catherine Skari

GENE THERAPY | FDA Decision on Lovo-cel for SCD Now Expected by Year’s End

The regulatory agency has agreed to review an application from lovo-cel’s developer, Bluebird Bio, requesting the gene therapy’s approval for SCD…

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PREGNANCY | Study Results Indicate AIHA in Pregnant Women Is Manageable

Among these patients, however, close monitoring, the administration of therapy when needed, and the awareness of potential complications, both for…

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Sickle Cell Disease Is 11 Times More Deadly Than Previously Recorded, Suggests Study

A new study suggests the number of deaths due to sickle cell disease is 11 times higher than what is…

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EHA2023 | MASP-3 Inhibitor Demonstrates Clinical Efficacy in Paroxysmal Nocturnal Hemoglobinuria

OMS906 led to transfusion independence in the majority of patients with PNH enrolled so far on the trial (n =…

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Examining Mental Health, Education, Employment, and Pain in Sickle Cell Disease

Importance: Pain related to sickle cell disease (SCD) is complex and associated with social determinants of health. Emotional and stress-related effects…

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Venous Thromboembolism Prophylaxis in Sickle Cell Disease: A Multicenter Cohort Study of Adolescent Inpatients

Patients with sickle cell disease (SCD) are predisposed to a hypercoagulable state. Despite the increased risk of venous thromboembolism in…

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Examining Mental Health, Education, Employment, and Pain in Sickle Cell Disease

Pain affects sickle cell disease (SCD) patients’ quality of life and functional ability. Βut what is the association of educational…

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POLICY NEWS | TIF Joins Important Policy Event in Brussels Ahead of New EU Rules on Blood, Tissue, Cells Approval

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EVENT | Rare Anaemias International Network (RAIN) Members Meeting – 16 June 2023

The members meeting was open to all RAIN members and their individual networks. This Meeting sought to: provide an update…

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