Catherine Skari

FDA APPROVES AQVESME™ (mitapivat) | First Oral Therapy for Anaemia Across All Forms of Thalassaemia

This regulatory decision marks a landmark milestone in the management of thalassaemia, as AQVESME is now the first and only…

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PUTTING PATIENTS FIRST IN CLINICAL RESEARCH | New EU Recommendations to Reduce Trials Bureaucracy

As Prof. Martin Dreyling, Chair of the Coalition for Reducing Bureaucracy, explains: “The current safety requirements for investigators are disproportionately…

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EU AGREES LANDMARK REFORM OF PHARMACEUTICAL LEGISLATION | What It Means for Patients and Public Health

 This milestone agreement — part of what has been referred to as the “pharma package” — was negotiated between the…

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National Thalassemia Registry: A 30-year Journey of implementing Carrier Screening in Singapore

Introduction Haemoglobinopathies, which include thalassemia and structural haemoglobin variants, are the most common inherited disease affecting an estimated 20% of…

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1st TIF NURSING WORKSHOP ON HAEMOGLOBINOPATHIES | 29-30 November 2025

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1st TIF NURSING WORKSHOP ON HAEMOGLOBINOPATHIES | 29-30 November 2025

📌 Workshop Title: 1st TIF Nursing Workshop on Haemoglobinopathies 📌 Date & Venue: Saturday & Sunday, 29-30 November 2025 |…

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β-Thalassemia Minor Is Associated With High Rates of Worsening Anemia in Pregnancy

Worsening of anemia because of β-thalassemia minor in pregnancy is not a well-known complication and, when acknowledged, is described as…

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TOPICS IN FOCUS SERIES | Guidelines for the Management of Thalassaemia Syndromes

Each booklet focuses on a specific aspect of the updated guidelines for transfusion-dependent thalassaemia (TDT), non-transfusion-dependent β-thalassaemia (NTDT), and α-thalassaemia,…

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ANNUAL REPORT 2024 | A Year of Resilience and Progress

It is a privilege to present the Federation’s Annual Report for 2024, capturing a year defined by resilience, innovation, and…

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Impact of Lifetime Anaemia and Iron Control on Outcomes in Β-Thalassaemia: Data from the Longitudinal de-LIGHT Study

Summary Evidence on the impact of anaemia and iron control on morbidity and mortality in β‐thalassaemia is limited to short‐term…

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