Catherine Skari
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Aug- 2021 -18 AugustScientific Literature
How to Facilitate Decision-Making for Hematopoietic Stem Cell Transplantation in Patients With Hemoglobinopathies. The Perspectives of Healthcare Professionals
Hematopoietic stem cell transplantation decision-making for hemoglobinopathy patients is a complex process, and it remains difficult for health care professionals…
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Jun- 2021 -28 JuneScientific Literature
The European Medicines Agency Review of Crizanlizumab for the Prevention of Recurrent Vaso-Occlusive Crises in Patients With Sickle Cell Disease
Crizanlizumab is a monoclonal antibody that binds to P-selectin. On October 28, 2020, a conditional marketing authorization valid through the…
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7 JuneScientific Literature
Economic Evaluation of Betibeglogene Autotemcel (Beti-cel) Gene Addition Therapy in Transfusion-Dependent β-Thalassemia
Background: Standard of care (SoC) for transfusion-dependent β-thalassemia (TDT) requires lifelong, regular blood transfusions as well as chelation to reduce…
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1 JuneScientific Literature
Research in Sickle Cell Disease: From Bedside to Bench to Bedside
Sickle cell disease (SCD) is an exemplar of bidirectional translational research, starting with a remarkable astute observation of the abnormally…
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1 JuneScientific Literature
Innovative Treatments for Rare Anemias
Rare anemias (RA) are mostly hereditary disorders with low prevalence and a broad spectrum of clinical severity, affecting different stages…
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Apr- 2021 -22 AprilScientific Literature
Survival and Causes of Death in 2,033 Patients with Non-Transfusion-Dependent β-Thalassemia
Non-transfusion-dependent β-thalassemia (NTDT) is a broad term encompassing patients who do not require lifelong transfusion therapy for survival. Our understanding…
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22 AprilScientific Literature
Survival and Causes of Death in 2,033 Patients with Non-Transfusion-Dependent β-Thalassemia
Non-transfusion-dependent β-thalassemia (NTDT) is a broad term encompassing patients who do not require lifelong transfusion therapy for survival. Our understanding…
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Mar- 2021 -15 MarchScientific Literature
Setting up and Sustaining Blood and Marrow Transplant Services for Children in Middle-Income Economies: An Experience-Driven Position Paper on Behalf of the EBMT PDWP
Severe blood disorders and cancer are the leading cause of death and disability from noncommunicable diseases in the global pediatric…
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Feb- 2021 -20 FebruaryScientific Literature
Hydroxyurea Use Among Children With Sickle Cell Disease at King Abdulaziz University Hospital in Jeddah City
Background Sickle cell disease (SCD) is an autosomal recessive hemoglobinopathy that is very common and causes a great burden in…
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3 FebruaryScientific Literature
Assessment of Subclinical Renal Glomerular and Tubular Dysfunction in Children with Beta Thalassemia Major
Background: A good survival rate among patients with beta thalassemia major (beta-TM) has led to the appearance of an unrecognized…
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