Catherine Skari

TURNING WEAKNESS TO STRENGTH by Dr Narongdej Poonsombudloet

”My story is dedicated to my parents and everything they have done for me. When I was 6 months old,…

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A CHANGE OF PERSPECTIVE by Milanpreet Kaur

”I consider it as divine intervention that this year’s theme resonated so well that it gave me immense strength and…

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NEW TREATMENTS | Gene Editing, mRNA Hold Promise as Fanconi Anemia Therapies

That is the major finding of a newly published review that examined how a better understanding in the scientific and…

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THE ECONOMIST | Dr Androulla Eleftheriou Discusses the Future of Thalassaemia Care

As genomics research moves from the bench to the bedside, clinical applications of genomics will affect even more areas of…

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CLINICAL NEWS | Novartis Releases Data for Potentially “Practice-Changing” PNH Medicine

The results, announced via news release, were presented at the 49th Annual Meeting of the European Society for Blood and…

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PK DEFICIENCY | New Episode of ‘Just Listen’ Podcast Out Now

Check out the latest episode of ‘Just Listen: Voices of PK Deficiency’ podcast, where host Dr Rachael Grace converses with…

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APLASTIC ANEMIA | Eltrombopag May Increase Complete Response Rate Among Pediatric Patients

The standards of care for aplastic anemia are allogeneic hematopoietic stem cell transplantation (HSCT) or immunosuppression with horse antithymocyte globulin…

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Guidelines for the Management of Non-Transfusion-Dependent β-Thalassaemia (3rd edition – 2023)

Ali T. Taher, MD PhD FRCP Khaled M. Musallam, MD PhD Maria Domenica Cappellini, MD FACP

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Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical Trials

Beta thalassaemia is an inherited disorder that impairs the production of haemoglobin, the blood protein responsible for transporting oxygen. Patients…

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Increased Risk of Venous Thromboembolism in Splenectomized Patients with Sickle Cell Disease

Sickle cell disease (SCD) patients may need to have their spleen removed due to various conditions related to their health…

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