Catherine Skari
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Sep- 2026 -9 SeptemberScientific Literature
Gene Therapy for Sickle Cell Disease: Practice Recommendations from the American Society for Transplantation and Cellular Therapy and the International Society for Cell & Gene Therapy
Abstract Gene therapy has emerged as a transformative treatment option for individuals with sickle cell disease (SCD), with recent regulatory…
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9 SeptemberScientific Literature
Osteoporosis Risk in Alpha and Beta Thalassemia: An Age- and Sex-Specific Retrospective Cohort Study
Abstract Summary Rationale: Differential skeletal risks between alpha- and beta-thalassemia subtypes remain unclear. Main result: Beta-thalassemia correlates with higher fracture…
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9 SeptemberScientific Literature
Addressing Obstetric and Gynecologic Needs in Thalassemia
Abstract Thalassemia represents a spectrum of rare, inherited blood disorders associated with a range of disease- and treatment-related complications. Thalassemia…
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9 SeptemberScientific Literature
Diagnosis and Management of Transfusion-Dependent Thalassemia: Evidence-Based Guidelines From the Pediatric Hematology Oncology Chapter of the Indian Academy of Pediatrics
Justification India bears a high burden of thalassemia, underscoring the need for enhanced awareness, systematic screening, and standardized, high-quality care.…
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8 SeptemberNews
TIF Annual General Assembly & Capacity Building Workshop 20–22 November 2026 | Athens, Greece
From 20 to 22 November 2026, the Thalassaemia International Federation (TIF) will convene its Annual General Assembly (AGA) and Capacity…
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8 SeptemberScientific Literature
Short- and Long-Term Effects of Transfusion in Β-Thalassemia: A Longitudinal Study of Transfusion Efficiency Factors
Abstract The complex interplay between donor and recipient factors likely influences transfusion outcomes in transfusion-dependent thalassemia (TDT). We investigated physiological…
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8 SeptemberScientific Literature
Experiences of Families With Children Diagnosed With Beta-Thalassemia: A Meta-Synthesis of Qualitative Studies
Background and purpose This meta-synthesis aimed to integrate qualitative studies examining the emotional, social, and practical experiences of families caring…
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8 SeptemberScientific Literature
Family Empowerment Education Module for Parents of Children With Thalassemia Major: A Randomized Controlled Study on Anxiety, Problem-Solving, and Psychological Resilience
Abstract Objective: This study determined the effect of the Family Empowerment in Pediatric Thalassemia Care (FE-PTC) Module on anxiety, problem-solving skills…
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8 SeptemberScientific Literature
Transition from Pediatric to Adult Care in Patients with Transfusion-Dependent Beta-Thalassemia in France: A National Study Concerning a Rare Disease
Abstract Background/Objectives: Transfusion-dependent β-thalassaemia (TDT) is a lifelong condition requiring coordinated multidisciplinary care. In France, where the disease is rare,…
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8 SeptemberScientific Literature
Dapagliflozin in Patients with Homozygous β-Thalassemia and Albuminuria
Abstract Patients with homozygous β-thalassemia show continuously improved survival, which has contributed to the development of kidney complications, predominantly expressed…
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