Catherine Skari
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Sep- 2022 -28 SeptemberNews
ADVANCED THERAPIES | Vertex, CRISPR To Submit Exa-Cel to FDA For β-Thalassaemia And Sickle Cell Disease
Vertex will submit its biologics licensing application (BLA) for exa-cel for rolling review, beginning in November 2022 and expects to…
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22 SeptemberNews
CDC | Many Children With Sickle Cell Anaemia In The US Not Receiving Lifesaving Screening And Treatment
According to a recent CDC study, fewer than half children with the disease in the US get the necessary screening,…
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19 SeptemberNews
CLINICAL NEWS | PYRUKYND® Receives Positive CHMP Opinion For The Treatment of PKD in Adults
PYRUKYND® is a first-in-class, oral PK activator that was recently approved by the U.S. Food and Drug Administration (FDA). If approved by the…
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15 SeptemberScientific Literature
Renal Dysfunction in Pediatric Patients in Iraq With β-Thalassemia Major and Intermedia
Background: With optimum transfusion and chelation therapy, the survival of β-thalassemia patients and the incidence of various complications, including renal…
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8 September
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8 SeptemberNews
SAFER BLOOD | EU Patients Have Begun Receiving Transfusions With Hemanext ONE® RBC Processing & Storage System
Doctors have begun transfusing patients suffering from hematological malignancies using RBCs processed and stored with the Hemanext ONE® system, as part…
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2 SeptemberScientific Literature
Precision Medicine and Sickle Cell Disease
Sickle cell disease (SCD) is characterized by variable clinical outcomes, with some patients suffering life-threatening complications during childhood, and others…
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Aug- 2022 -30 AugustScientific Literature
Does Hepcidin Tuning Have a Role Among Emerging Treatments for Thalassemia?
The treatments available for thalassemia are rapidly evolving, with major advances made in gene therapy and the modulation of erythropoiesis.…
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29 August
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29 AugustNews
SICKLE CELL DISEASE | African Health Ministers Launch Drive to Curb SCD’s Toll
This effort, backed by the African Regional Office of the World Health Organization (WHO), aims to curb SCD΄s toll in…
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