Catherine Skari

BREAKING NEWS | TIF Applauds the EU Parliament’s Adoption of the SoHO Regulation

The new rules modernize the existing directives, now two decades old, and are aimed at addressing challenges and weaknesses identified…

Read More »

People with Thalassaemia Can Achieve Anything!

Read More »

Climbing Beyond Limits: How I Defied Thalassaemia and Embraced Life

Read More »

Unstoppable Spirit: From Thalassaemia Warrior to Advocate for Change

Read More »

Thalassemia and Taiwan: A Journey of Discovery

Read More »

Defining Curative Endpoints for Transfusion-Dependent β-Thalassemia in the Era of Gene Therapy and Gene Editing

β-thalassemia is a monogenic disease that results in varying degrees of anemia. In the most severe form, known as transfusion-dependent…

Read More »

A Father’s Unyielding Spirit in the Face of Thalassaemia

Read More »

Systematic Review and Evidence Gap Assessment of the Clinical, Quality of Life, and Economic Burden of Alpha-Thalassemia

A recent evidence gaps assessment of the clinical, health-related quality of life, and economic burden associated with α-thalassemia is lacking.…

Read More »

Celebrating 54 Years of Living with Thalassemia and Still Thriving!

Read More »

REGULATORY NEWS | EMA Accepts Rocket Pharma’s Gene Therapy Application for Fanconi Anemia

RP-L102 is a gene therapy containing autologous hematopoietic stem cells that have been modified to contain a functional copy of…

Read More »