Catherine Skari

Health‑Related Quality‑of‑Life Impacts Associated with Transfusion‑Dependent β‑Thalassemia in the USA and UK: A Qualitative Assessment

Background: Individuals living with transfusion-dependent β-thalassemia (TDT) experience reduced health-related quality of life due to fatigue and chronic pain, which…

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JUST LISTEN | Voices of PK Deficiency Episode on the Impact of New International Standards

Host Dr. Rachael Grace is joined by Tamara Schryver of Thrive with Pyruvate Kinase Deficiency and Alejandra Watson from the…

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Guideline for the Management of Conception and Pregnancy in Thalassaemia Syndromes: A British Society for Haematology Guideline

This comprehensive guideline, developed by a representative group of UK-based medical experts specialising in haemoglobinopathies, addresses the management of conception…

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Haemoglobinopathies and Other Rare Anemias in Spain: Ten Years of a Nationwide Registry (REHem-AR)

REHem-AR was created in 2013. The progressive implementation of neonatal screening for haemoglobinopathies in Spanish autonomous communities where the registry…

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How to Manage Thalassaemia During Pregnancy: Expert Advice from the BSH

A comprehensive multidisciplinary approach is essential for managing conception and pregnancy in patients with a variety of medical conditions, including…

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NEW APPROVAL | FDA Endorses Piasky for Paroxysmal Nocturnal Hemoglobinuria

Piasky, developed by Roche, is a monoclonal antibody that targets complement protein C5. Crovalimab binds to C5 to prevent its…

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Predicting Factors of Survival Rates Among α-and β-Thalassemia Patients: A Retrospective 10-Year Data Analysis

Background: Thalassemia is a genetic hemoglobinopathy in which a defective globin chain can cause transfusion-dependent anemia and other complications. As genotype…

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CAD | Enjaymo Not Cost-Effective at Current Price, According to US Study

This conclusion was drawn from a cost-effectiveness study utilizing data from the Phase 3 CARDINAL clinical trial, which backed the…

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