Catherine Skari
-
Nov- 2022 -7 novembreClinical News
NEW HOPE FOR THALASSAEMIA/SCD | UK Trial Of Lab Grown Red Blood Cells Begins
The Restore trial, led jointly by NHS Blood and Transplant and the University of Bristol, is studying the lifespan of the…
Lire la suite » -
Sep- 2022 -28 septembreActualités
ADVANCED THERAPIES | Vertex, CRISPR To Submit Exa-Cel to FDA For β-Thalassaemia And Sickle Cell Disease
Vertex will submit its biologics licensing application (BLA) for exa-cel for rolling review, beginning in November 2022 and expects to…
Lire la suite » -
22 septembreActualités
CDC | Many Children With Sickle Cell Anaemia In The US Not Receiving Lifesaving Screening And Treatment
According to a recent CDC study, fewer than half children with the disease in the US get the necessary screening,…
Lire la suite » -
19 septembreActualités
CLINICAL NEWS | PYRUKYND® Receives Positive CHMP Opinion For The Treatment of PKD in Adults
PYRUKYND® is a first-in-class, oral PK activator that was recently approved by the U.S. Food and Drug Administration (FDA). If approved by the…
Lire la suite » -
8 septembre
-
8 septembreActualités
SAFER BLOOD | EU Patients Have Begun Receiving Transfusions With Hemanext ONE® RBC Processing & Storage System
Doctors have begun transfusing patients suffering from hematological malignancies using RBCs processed and stored with the Hemanext ONE® system, as part…
Lire la suite » -
Août- 2022 -29 août
-
29 aoûtActualités
SICKLE CELL DISEASE | African Health Ministers Launch Drive to Curb SCD’s Toll
This effort, backed by the African Regional Office of the World Health Organization (WHO), aims to curb SCD΄s toll in…
Lire la suite » -
26 aoûtActualités
A HISTORIC BREAKTHROUGH | UNICEF Signs First-Ever Malaria Vaccine Supply Contract With GSK
The contract will enable UNICEF to deliver more than 18 million doses of the RTS,S vaccine – also known under…
Lire la suite » -
17 aoûtActualités
BREAKING NEWS | Bluebird’s Gene Therapy For β-Thalassaemia Wins US Approval
The green light is “monumental” for both patients and the company itself, Tom Klima, Bluebird’s Chief Commercial Officer, said in…
Lire la suite »
