New Therapies
What’s New In Clinical Trials for Thalassaemia and Sickle Cell Disease?
Clinical News
Novembre 6, 2020
What’s New In Clinical Trials for Thalassaemia and Sickle Cell Disease?
There is a lot of hustle and bustle in the scientific fields of thalassemia and sickle cell disease during the past few months, with many companies making remarkable progress in…
eThalED Webinar Series: Access to New Therapies – Reblozyl
Education
Giugno 18, 2020
eThalED Webinar Series: Access to New Therapies – Reblozyl
The 1st webinar for Medical Specialists organised in the context of TIF’s eThalED online course is here. Dr Antonio Piga, Professor of Paediatrics & Dean of the Medicine School at…
FDA Grants Orphan Drug Designation to Mitapivat for Treatment of Thalassaemia
Clinical News
Giugno 11, 2020
FDA Grants Orphan Drug Designation to Mitapivat for Treatment of Thalassaemia
Agios Pharmaceuticals Inc. announced that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug Designation to the company’s first-in-class pyruvate kinase-R (PKR) activator Mitapivat for the treatment of…