Surveys
Gene Therapy & Thalassaemia
29 Ιουνίου, 2020
Gene Therapy & Thalassaemia
Millions of people worldwide suffer from inherited non-malignant blood disorders like thalassaemia and sickle cell disease. The culprit: genetic defects in their blood stem cells. One of the novel…
Gene Therapy and Thalassaemia: The Patients’ Perspective survey!
15 Μαΐου, 2019
Gene Therapy and Thalassaemia: The Patients’ Perspective survey!
A significant number of gene therapy approaches are currently undergoing clinical trials, some of which are already producing encouraging results. The Bluebird Bio’s gene therapy product, under the name ZYNTEGLO™,…