Clinical Trial Updates (SCD)

ARU-1801 (gene therapy)

  • Product Information

    Product Information

    Scientific name: ARU-1801
    Brand name: Ν/Α
    RESPONSIBLE: Children’s Hospital Medical Center, Cincinnati, US

  • Clinical Trial/Study Information

    Clinical Trial/Study Information

    Last update: 22/6/2023

    Trial Name: Gene Transfer in Patients with SCD (MOMENTUM)
    Code: NCT02186418
    Phase: 1/2
    Eligible patient diagnosis: : SCD (adults) (age 18-45)
    No. of Patients enrolled: 7 [anticipated] (Last update: 17/11/2022)
    Study Sites: 1 Sites per country

    Completion date: June 2023
    Scope of the Study / Aim: Increase therapeutic haemoglobin ; decrease annual VOCs ; evaluate RIC melphalan conditioning (less toxic than myeloablative approaches

  • Regulatory Information

    Regulatory Information

    Status: Not Authorised


    Additional notable points:

    • EMA: N/A
    • FDA: N/A
    • MHRA: N/A

Update: 30 September 2023

No update available.


Update: 30 June 2023

No update available.


Update: 31 March 2023

No update available.

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