Clinical Trial Updates (SCD)
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Risto-cel
Update: 30 June 2026 Ristoglogene autogetemcel (risto-cel, BEAM-101), an investigational cell therapy using base editing enabling re-expression of γ-globin and production of anti-sickling fetal hemoglobin (HbF). Data presented at the…
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CSL889
Update: 30 June 2026 No update available. Update: 31 March 2026 No update available. Update: 22 December 2025 No update available. Update: 30 September 2025 No update…
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Pociredir
Update: 30 June 2026 Company has announced discontinuation due to FDA concerns regarding pociredir’s benefit-risk profile in SCD, stemming from an unexpectedly high rate of secondary hematologic malignancies observed with…
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Osivelotor
Update: 30 June 2026 • Data presented at the EHA Annual Congress (11 – 14 June 2026) from the phase 2 βportion of the phase 2/3 DREAM clinical trial reported…
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