الرئيسية » Clinical trial updates (صفحة 2)

Clinical trial updates

Gene Editing

CRISPR gene editing   Update: 25 November 2019 CRISPR Therapeutics and Vertex Pharmaceuticals announced positive, interim data from the first two patients with severe haemoglobinopathies treated with the investigational CRISPR/Cas9 gene-editing therapy CTX001. 1 patient with transfusion-dependent beta-thalassaemia (TDT) received CTX001 in the first quarter of 2019 and data for ...

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Hepcidin

Hepcidin trials – TRANSCEND   Update: 25 November 2019 No update available.   Update: 27 September 2019 No update available   Update: 30 July 2019 No update available.   Update: 30 May 2019 No update available.   Update: 01 February 2019 Hepcidin is a hormone that performs various functions related ...

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Improving safety of blood transfusion

    INTERCEPT-treated RBCs   Update: 25 November 2019 No update available   Update: 27 September 2019 No update available   Update: 30 July 2019 No update available.   Update: 30 May 2019 No update available.   Update: 01 February 2019 The SPARC study was a randomized, double blinded cross-over ...

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