News
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EHA2023 | MASP-3 Inhibitor Demonstrates Clinical Efficacy in Paroxysmal Nocturnal Hemoglobinuria
OMS906 led to transfusion independence in the majority of patients with PNH enrolled so far on the trial (n = 10). PNH, a rare and life-threatening blood disorder, is characterized…
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EVENT | Rare Anaemias International Network (RAIN) Members Meeting – 16 June 2023
The members meeting was open to all RAIN members and their individual networks. This Meeting sought to: provide an update and overview of the RAIN Steering Committee and Scientific Advisory…
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TIFLIX | Taking Thalassaemia Education To The Next Level
Watch Unlimited Videos from World-Renowned Experts This brand-new video library powered by TIF gathers a wealth of audiovisual content on everything you need to know about thalassaemia and sickle cell disease, presented to…
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NEW TREATMENTS | Gene Editing, mRNA Hold Promise as Fanconi Anemia Therapies
That is the major finding of a newly published review that examined how a better understanding in the scientific and molecular underpinnings of the disease has translated into potential new…
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THE ECONOMIST | Dr Androulla Eleftheriou Discusses the Future of Thalassaemia Care
As genomics research moves from the bench to the bedside, clinical applications of genomics will affect even more areas of medicine, improving disease prevention, diagnosis, and treatment. Today, it is…
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CLINICAL NEWS | Novartis Releases Data for Potentially “Practice-Changing” PNH Medicine
The results, announced via news release, were presented at the 49th Annual Meeting of the European Society for Blood and Marrow Transplantation in Paris. “The APPOINT-PNH results are consistent with…
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PK DEFICIENCY | New Episode of ‘Just Listen’ Podcast Out Now
Check out the latest episode of ‘Just Listen: Voices of PK Deficiency’ podcast, where host Dr Rachael Grace converses with Dr Matthew Heeney, a haematologist whose research is focused on the…
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